Organization |
We are a nonprofit-organization aimed at fostering breakthrough research that make an important difference in the lives of patients and their family members. Our actions are performed at the national and international level.
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Vision |
The Portuguese Association for CDG and other Rare Metabolic Diseases (APCDG-DMR) vision is based on the belief of its founder to achieve the hopes of patients and families who suffer from rare diseases, key stakeholders need:
This is a very promising and innovative approach whereby all parties combine their strength and expertise in a collaborative, dynamic and shared spirit. That is the key driver to achieving transformative, potentially life-saving therapies that can revolutionize the clinical treatment of a disease and offer new life to patients and concerned families. |
Mission |
We strive to have a patient-focused drug development.
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CommitmentWe are committed to advancing progress by transforming the current research into meaningful research and drug development programs. Our major priority is to provide a complete and holistic view of the patient as a person.
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FocusOur focus is the inclusion of patients and patient advocacy groups as an essential component in the development of successfully clinical programs. The rare disease community is our inspiration.
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Core Values |
Our core values reflect our capacity to define what needs to be done in order to boost development of therapies that will produce a significant benefit for patients and their family members.
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Learship |
APCDG-DMR is a nonprofit-organization aimed at fostering breakthrough research that makes a difference in the lives of patients and their family members.
Our actions are performed at the national and international level. Exceptional individuals are doing tremendous contributions as volunteers to move APCDG mission moving forward. Several working groups have been created across several domains committed to address the concerns of affected families. |